Organization Overview
Alternative names
Anemia, Sickle Cell (Phase 1)
Cystinosis (Phase 2)
Diabetes Mellitus (Phase 2)
Diabetes Mellitus, Type 1 (Phase 2)
Lymphoma (Phase 1)
Lysosomal Storage Diseases (Phase 2)
Multiple Myeloma (Phase 1)
Retinitis (Phase 2)
Retinitis Pigmentosa (Phase 2)