Organization Overview
Alternative names
Immunologic Deficiency Syndromes (Phase 3)
Leukodystrophy, Metachromatic (Phase 3)
Lysosomal Storage Diseases (Phase 3)
Mucopolysaccharidoses (Phase 2)
Mucopolysaccharidosis III (Phase 2)
Severe Combined Immunodeficiency (Phase 3)
Syndrome (Phase 2)
Wiskott-Aldrich Syndrome (Phase 2)