Clinical Drug Experience Knowledgebase

Amino Acid Metabolism, Inborn Errors (Phase 2)

Aniridia (Phase 2)

Ataxia (Phase 3)

Breast Neoplasms (Phase 1)

Carcinoma, Ovarian Epithelial (Phase 1)

Central Nervous System Neoplasms (Phase 1)

Cerebellar Ataxia (Phase 3)

Coronavirus Infections (Phase 3)

Cystic Fibrosis (Phase 3)

Drug Resistant Epilepsy (Phase 3)

Endometrial Neoplasms (Phase 2)

Epilepsies, Myoclonic (Phase 2)

Epilepsy (Phase 3)

Fibrosis (Phase 3)

Friedreich Ataxia (Phase 3)

Genetic Diseases, Inborn (Phase 3)

Genetic Diseases, X-Linked (Phase 3)

Glioma (Phase 1)

Hemophilia A (Phase 2)

Hemophilia B (Phase 2)

Leiomyosarcoma (Phase 1)

Leukemia (Phase 1)

Leukemia, Myeloid (Phase 1)

Leukemia, Myeloid, Acute (Phase 1)

Metabolism, Inborn Errors (Phase 2)

Mitochondrial Diseases (Phase 3)

Muscular Diseases (Phase 3)

Muscular Disorders, Atrophic (Phase 3)

Muscular Dystrophies (Phase 3)

Muscular Dystrophies, Limb-Girdle (Phase 3)

Muscular Dystrophy, Duchenne (Phase 3)

Musculoskeletal Diseases (Phase 3)

Neoplasms (Phase 1)

Nervous System Diseases (Phase 3)

Nervous System Neoplasms (Phase 1)

Neurofibroma (Phase 2)

Neurofibromatoses (Phase 2)

Neurofibromatosis 1 (Phase 2)

Neurofibromatosis 2 (Phase 2)

Neuromuscular Diseases (Phase 3)

Ovarian Neoplasms (Phase 1)

Pneumonia (Phase 3)

Sarcoma (Phase 2)

Sarcoma, Kaposi (Phase 2)