Diseases [C] » Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16] » Genetic Diseases, Inborn » Metabolism, Inborn Errors » Amyloidosis, Familial
Diseases [C] » Nutritional and Metabolic Diseases [C18] » Metabolic Diseases » Metabolism, Inborn Errors » Amyloidosis, Familial
Diseases [C] » Nutritional and Metabolic Diseases [C18] » Metabolic Diseases » Proteostasis Deficiencies » Amyloidosis » Amyloidosis, Familial
Description
Diseases in which there is a familial pattern of AMYLOIDOSIS. MeSH
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Subtype Terms (2)
Amyloid Neuropathies, Familial
6 drugs (3 approved, 3 experimental)
Phase 3 Indicated Drugs (4)
Other Experimental Indicated Drugs (1)
Organization Involved with Phase 3 Indications (4)
Organization Involved with Other Experimental Indications (1)
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UMLS Data
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